This presentation is intended to walk you through the journey that started over 50 years ago with the beginnings of gene therapy research. We will walk through the basics of genetics and how that plays a role in hemophilia. With that knowledge, we will look at how gene therapy is meant to work, and discuss both the potential for and the challenges of investigational gene therapy research today.
Speaker: Laureen Temple, Senior Patient Education Liaison
HFM will treat attendees to dinner during this educational program.
Please note, Spark Therapeutics is not affiliated with the meals provided by HFM. Order carryout or delivery and send a photo of your itemized receipt to Laura at firstname.lastname@example.org. You will be reimbursed for your meal (up to $30 per family). Please note that we are unable to reimburse alcohol purchases.
HFM does not endorse any specific product or company.